Mutations in the MECP2 gene — which typically underlie Rett syndrome — cause problems in how neurons, or nerve…
Articles by Margarida Maia, PhD
Blocking a small RNA molecule that helps control whether certain genes are switched on or off reactivated the healthy copy…
NTI164, a cannabis-based oil being developed by Neurotech International, may help girls with Rett syndrome communicate more easily, enjoy…
Early changes in speech, including fewer varied sounds, may signal Rett syndrome before obvious developmental delays and this may…
Into-the-nose delivery of a solution containing clinical-grade human nerve growth factor (NGF) improved cognitive and motor function in a mouse…
Researchers used tiny, magnetic spheres to deliver a gene editing toolbox into stem cells prepared from a patient’s skin sample…
TSHA-102, an experimental gene therapy for Rett syndrome, appears to be well tolerated and may be of benefit in multiple…
The first episode of “Magnolia’s Guide to Adventuring,” a documentary series that follows people with Rett syndrome and…
Taysha Gene Therapies has received the needed approval to move forward with dose escalation in its Phase 1/2 trial testing…
An injection of Taysha Gene Therapies’ experimental gene therapy TSHA-102 into the spinal canal of young mice…