Experimental treatments
for Rett Syndrome

Overview

Several experimental therapies for Rett syndrome are currently undergoing clinical testing. Current experimental approaches include gene therapies as well as targeted therapies that aim to support nerve cell health.

Blarcamesine

Blarcamesine (Anavex 2-73) is an oral therapy designed to activate a protein called sigma-1 receptor to help proteins fold properly and improve nerve cell health.

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