Joe Pierce,  —

Rare Disease Day 2023

Recent Posts

• 1st analysis of global Rett prevalence may help in trial planning
• At-home physical therapy program strengthens patients’ motor skills
• FDA approves trofinetide, now Daybue, as 1st treatment for Rett
• Slower, shorter steps found for Rett patients in 3D gait analysis
• I trust the system to do the caregiving when I can’t
• Touchless Emerald AI biosensor gets $1.1M funding boost from RSRT
• Plans for initial trial of oral RVL001 in Rett syndrome patients advancing
• A birthday wish for the sibling of a child with special needs
• Rett Syndrome Research Trust nets $500K to study Emerald biosensor
• FDA grants orphan drug designation to Ketarx for Rett syndrome