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• Early study offers framework for developing Rett gene therapies
• The last 24 hours with my oldest daughter, who had Rett syndrome
• Problems in how nerve cells degrade waste may underlie Rett, study finds
• ID’d microRNAs may serve as Rett disease progression biomarkers
• Marvel’s MB204 improves social behaviors in Rett mice in study
• Rett girl has severe immune reaction to high dose of NGN-401
• Our daughter’s wings helped runners fly across the finish line
• Meaningful gains in skills seen with Rett gene therapy in trial: Data
• Intranasal delivery of human NGF eases Rett symptoms in mice
• Female Rett syndrome mouse model mimics patient gene dysregulation