The Rett Syndrome Research Trust (RSRT) is teaming up with partners in industry and academia to get ready for…
Articles by Marisa Wexler, MS
The first girl with Rett syndrome has been given the experimental gene therapy TSHA-102 in a clinical trial, according…
Treatment with Anavex 2-73 (blarcamesine) led to improvements in behavior among children with Rett syndrome in a Phase 2/3…
Rett syndrome is marked by unusually low levels of LAT1, a protein that’s needed to move amino acids —…
Electrically stimulating a specific region of the brain led to improvements in memory in a mouse model of Rett…
Treatment with a modified version of a signaling molecule called NGF improved survival and normalized behavior in a mouse model…
A second adult with Rett syndrome has been given the experimental gene therapy TSHA-102 in an ongoing clinical trial,…
Girls with Rett syndrome have detectable abnormalities in the electrical activity in their brains, a new study confirms. The…
Repetitive movements of rubbing the hands together are associated with an increased risk of skin injuries in people with…
The first woman with Rett syndrome given the gene therapy TSHA-102 has experienced improvements in her sleep, breathing, and…