The Rett Syndrome Research Trust (RSRT) has received a $1 million donation to help develop a cure for…
Articles by Marisa Wexler, MS
Novartis announced it is scrapping plans to move OAV201, an investigational gene therapy for Rett syndrome, into clinical…
The International Rett Syndrome Foundation (IRSF), an organization focused on accelerating research to treat and cure Rett syndrome,…
Abnormally slow or shallow breathing in Rett syndrome develops in part due to altered inhibitory signals in the brain,…
Participating in school virtually — using a computer with a webcam — is socially and cognitively engaging for people with…
Acadia Pharmaceuticals is launching an open-label clinical trial of its oral investigational medication trofinetide in toddlers and young girls…
Acadia Pharmaceuticals has completed enrollment in the Phase 3 clinical trial LAVENDER, which is testing the investigational medication…
The Ontario Rett Syndrome Association (ORSA) announced the awarding of two grants to support research into Rett syndrome in…
A music-based intervention helped to normalize certain social behaviors in a mouse model of Rett syndrome, researchers reported. Findings also…
Alcyone Therapeutics, a new company focused on developing gene therapies for disorders that affect the nervous system, announced its…