All 12 girls and women with Rett syndrome given the gene therapy candidate TSHA-102 in a clinical trial gained…
Articles by Steve Bryson, PhD
Stimulating the vagus nerve, part of the autonomic nervous system that regulates involuntary functions, paired with sound tones, may support…
Fenfluramine, an add-on medication already approved for certain types of epilepsy, may also help to reduce the frequency of hard-to-treat…
MIT researchers have discovered that tiny blood vessels in the brains of people with Rett syndrome may be more…
Modulating nerve cells to boost production of the mutant form of the MeCP2 protein that causes most cases of…
While early brain structures appear to form normally in Rett syndrome, problems emerge later as brain cells grow, move,…
In Rett syndrome, certain brain cells that form before birth and mature slowly remain immature and do not develop…
Partially restoring the production of MeCP2, the protein deficient in people with Rett syndrome, reversed abnormal nerve signaling in…
The U.S. Food and Drug Administration (FDA) has approved Daybue Stix (trofinetide), a dye- and preservative-free powder formulation of…
One year of daily Daybue (trofinetide) treatment led to improvements in behaviors such as nonverbal communication, alertness, and social…