Taysha Gene Therapies received $95 million in funding that will support the clinical development of its gene therapy…
Articles by Patricia Inácio, PhD
A Phase 2/3 trial evaluating the treatment candidate Anavex-2-73 (blarcamesine) in children and adolescents with Rett syndrome has started…
Researchers have discovered that early inactivation of the X chromosome is a two-step process regulated by two different genetic…
Taysha Gene Therapies has raised $30 million and established a partnership with UT Southwestern Medical Center to expand…
Anavex Life Sciences announced plans to continue to screen and enroll patients into its active trials for Rett…
The number of treatments for children with rare diseases has grown over the past decade, according to a new study. However,…
Scientists in Iran have identified two new mutations in the MECP2 gene in two young girls with Rett…
Parents of adolescents with Rett syndrome and other neurological or psychiatric conditions are open to treatment with deep…
Genes that are normally silenced in the X-chromosome transition from an “off’ to an “on” state at different speeds, an…
Anavex Life Sciences is launching a clinical trial to assess the safety and efficacy of its small molecule therapy…