A new mutation has been found in the MECP2 gene — associated with most Rett syndrome cases — in…
Articles by Vanda Pinto, PhD
Taysha Gene Therapies is partnering with Astellas Pharma to support the development of its gene therapy programs for…
The Rett Syndrome Research Trust (RSRT) has received a large donation from SANTÉ Realty Investments, a provider of…
The U.S. Food and Drug Administration (FDA) has granted rare pediatric disease and orphan drug designations to DepYmed’s orally…
The International Rett Syndrome Foundation (IRSF) has seen its federal funding efforts rewarded in the U.S. as a bill…
A six-month intensive and individualized exercise program prevented the progression of scoliosis, a sideways curvature of the spine, in most girls…
Neurons activated at the same time — a state called neuronal synchrony — and with lesser complexity in the relationships…
Stem cells engineered to produce a constant level of a downstream target of the MECP2 protein, called brain-derived neurotrophic factor…
Treatment with fluoxetine, a type of antidepressant sold under the brand name Prozac, increased the number of cells producing…
Shape Therapeutics has raised $112 million in financing to support work into developing its portfolio of RNA technologies to…