Patients with Rett syndrome have similar spinal surgery outcomes to those of people with cerebral palsy (CP), according…
Articles by Forest Ray PhD
Same But Different, a U.K. nonprofit that uses the arts to bring communities together, is holding a calendar photography…
Raremark, an online rare disease patient community, has launched a digital platform called Xperiome, aimed at streamlining the…
Mutations in the MECP2 gene, which lead to most cases of Rett syndrome, prevent the formation of droplet-like…
For the first time, scientists have repaired a mutation in mice that underlies Rett syndrome, partially restoring lost protein…
By targeting a protein called BRD4, an experimental cancer treatment known as JQ1Â reversed cellular abnormalities and extended survival…
The EveryLife Foundation for Rare Diseases has launched a nationwide National Burden of Rare Disease Survey to measure…
The Alexion Charitable Foundation has awarded $1.1 million in grants to programs that support those with rare diseases during…
Acadia Pharmaceuticals is again enrolling in its Phase 3 LAVENDER trial testing trofinetide as a treatment for girls…
The Black Women’s Health Imperative (BWHI) recently created a Rare Disease Diversity Coalition focused on reducing racial disparities in…